Absence of Efficacy of Everolimus in Neurofibromatosis 1-Related Plexiform Neurofibromas: Results from a Phase 2a Trial.
J Invest Dermatol. 2019;139(3):718-720.
MeSH terms: Adult; Everolimus; Female; Follow-Up Studies; Humans; Immunosuppressive Agents; Magnetic Resonance Imaging; Male; Neurofibroma, Plexiform; Neurofibromatosis 1; Young Adult
DOI: 10.1016/j.jid.2018.09.016